The success of gene therapy requires the safe and effective delivery of genetic material into affected cells using a suitable vector. Several gene and cell therapy therapies have already received FDA approval to treat various symptoms, including neuromuscular symptoms, inherited forms of blindness and certain blood cancers.
These cutting-edge therapies might benefit greatly from innovations in gene therapy techniques.
This listicle is available for download to explore recent advances in gene therapy, such as:
- Novel virus-free delivery systems
- Precision targeting using lipid nanoparticles
- Safer gene editing systems
